Ataluren, a new therapeutic for alpha-1 antitrypsin-deficient individuals with nonsense mutations

Academic Article

Digital Object Identifier (doi)

Author List

  • Reeves EP; O'Dwyer CA; Dunlea DM; Wormald MR; Hawkins P; Alfares M; Kotton DN; Rowe SM; Wilson AA; McElvaney NG

    • Start Page

  • 1099

    • End Page

  • 1102

    • Volume

  • 198

    • Issue

  • 8