An Open Label N of 1 Study to Evaluate the Safety and Efficacy of Long-Term Treatment with Ivacaftor in Combination with ALTALUREN (PTCD124) In Subjects with Nonsense Mutation Cystic Fibrosis


Total Award Amount

  • 51500.00
  • Direct Costs

  • 46818.00
  • Sponsor Award Id

  • MDBR-16-120-CF1282x
  • Contributor

  • George Solomon   Investigator  
  • Heather Hathorne   Investigator  
  • Steven Rowe   Principal Investigator