Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease

Academic Article

Authors

Published In

  • Molecular Therapy  Journal
  • Digital Object Identifier (doi)

    Pubmed Id

  • 25695099
  • Author List

  • Li Y; Miller CA; Shea LK; Jiang X; Guzman MA; Chandler RJ; Ramakrishnan SM; Smith SN; Venditti CP; Vogler CA
  • Start Page

  • 691
  • End Page

  • 701
  • Volume

  • 29
  • Issue

  • 2